Gene therapy for Leber congenital amaurosis

Adv Exp Med Biol. 2003:533:415-22. doi: 10.1007/978-1-4615-0067-4_53.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.
  • Review

MeSH terms

  • Blindness / congenital
  • Blindness / therapy*
  • Carrier Proteins
  • Eye Proteins
  • Genetic Therapy*
  • Humans
  • Mutation
  • Optic Atrophy, Hereditary, Leber / therapy*
  • Proteins / genetics
  • cis-trans-Isomerases

Substances

  • Carrier Proteins
  • Eye Proteins
  • Proteins
  • retinoid isomerohydrolase
  • cis-trans-Isomerases