Neurological diseases and RNA-directed gene regulation: prospects for new diagnostics and therapy

Expert Rev Mol Diagn. 2003 May;3(3):269-74. doi: 10.1586/14737159.3.3.269.
No abstract available

Publication types

  • Editorial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alternative Splicing
  • Gene Expression Regulation*
  • Genes, Dominant
  • Genes, Recessive
  • Humans
  • Models, Genetic
  • Muscles / pathology
  • Mutation
  • Nervous System Diseases / diagnosis
  • Nervous System Diseases / genetics*
  • Nervous System Diseases / pathology
  • Nervous System Diseases / therapy
  • Neurons / pathology
  • RNA / genetics*
  • RNA-Binding Proteins / metabolism
  • Ribonucleoproteins / metabolism
  • Trinucleotide Repeat Expansion* / genetics

Substances

  • RNA-Binding Proteins
  • Ribonucleoproteins
  • RNA