Identification of a novel mutation in the GLUT2 gene in a patient with Fanconi-Bickel syndrome presenting with neonatal diabetes mellitus and galactosaemia

Eur J Pediatr. 2002 Jun;161(6):351-3. doi: 10.1007/s00431-002-0931-y. Epub 2002 Apr 16.

Abstract

We describe a patient with Fanconi-Bickel syndrome diagnosed by clinical manifestations and the identification of a novel mutation in the GLUT 2 gene. She was initially diagnosed with neonatal diabetes mellitus due to hyperglycaemia and glycosuria at 3 days of life. In addition, newborn screening for galactosaemia revealed hypergalactosaemia. Thereafter, she was managed with lactose-free milk and insulin therapy. However, she failed to grow and her liver became progressively enlarged. Her liver function deteriorated with increased prothrombin time. A liver biopsy done at age 9 months showed micronodular cirrhosis with marked fatty changes and she succumbed to hepatic failure with pneumonia at 10 months of age. DNA sequencing analysis of the GLUT 2 gene using her genomic DNA revealed a novel mutation in codon 5, lysine5 stop(K5X).

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Diabetes Mellitus / blood
  • Diabetes Mellitus / genetics*
  • Diabetes Mellitus / therapy
  • Fanconi Syndrome / genetics*
  • Fanconi Syndrome / physiopathology
  • Galactose / blood
  • Gene Expression Regulation
  • Glucose Transporter Type 2
  • Glycogen Storage Disease / genetics
  • Glycogen Storage Disease / pathology
  • Humans
  • Infant
  • Liver / physiopathology
  • Monosaccharide Transport Proteins / genetics*
  • Mutation

Substances

  • Glucose Transporter Type 2
  • Monosaccharide Transport Proteins
  • Galactose