A multicenter, open-label phase 3 study of emicizumab prophylaxis in children with hemophilia A with inhibitors.
Young G, Liesner R, Chang T, Sidonio R, Oldenburg J, Jiménez-Yuste V, Mahlangu J, Kruse-Jarres R, Wang M, Uguen M, Doral MY, Wright LY, Schmitt C, Levy GG, Shima M, Mancuso ME.
Young G, et al.
Blood. 2019 Dec 12;134(24):2127-2138. doi: 10.1182/blood.2019001869.
Blood. 2019.
PMID: 31697801
Free PMC article.
Clinical Trial.