Comprehensive and long-term outcomes of enzyme replacement therapy followed by stem cell transplantation in children with Gaucher disease type 1 and 3.
Anurathapan U, Tim-Aroon T, Zhang W, Sanpote W, Wongrungsri S, Khunin N, Chutipongtanate S, Chirdkiatgumchai V, Ngiwsara L, Jaovisidha S, Khongkraparn A, Pakakasama S, Svasti J, Setchell KDR, Wattanasirichaigoon D, Hongeng S.
Anurathapan U, et al. Among authors: wattanasirichaigoon d.
Pediatr Blood Cancer. 2023 Mar;70(3):e30149. doi: 10.1002/pbc.30149. Epub 2022 Dec 23.
Pediatr Blood Cancer. 2023.
PMID: 36562549