Personalized Development of Antisense Oligonucleotides for Exon Skipping Restores Type XVII Collagen Expression in Junctional Epidermolysis Bullosa.
Ablinger M, Lettner T, Friedl N, Potocki H, Palmetzhofer T, Koller U, Illmer J, Liemberger B, Hainzl S, Klausegger A, Reisenberger M, Lambert J, Van Gele M, Desmet E, Van Maelsaeke E, Wimmer M, Zauner R, Bauer JW, Wally V.
Ablinger M, et al. Among authors: van gele m.
Int J Mol Sci. 2021 Mar 24;22(7):3326. doi: 10.3390/ijms22073326.
Int J Mol Sci. 2021.
PMID: 33805154
Free PMC article.