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Measuring Fatigue and Fatigability in Spinal Muscular Atrophy (SMA): Challenges and Opportunities.
J Clin Med. 2023 May 14;12(10):3458. doi: 10.3390/jcm12103458.
J Clin Med. 2023.
PMID: 37240564
Free PMC article.
Review.
Neuroanatomical Models of Muscle Strength and Relationship to Ambulatory Function in Spinal Muscular Atrophy.
Rodriguez-Torres R, Fabiano J, Goodwin A, Rao AK, Kinirons S, De Vivo D, Montes J.
Rodriguez-Torres R, et al.
J Neuromuscul Dis. 2020;7(4):459-466. doi: 10.3233/JND-200550.
J Neuromuscul Dis. 2020.
PMID: 32925091
Free PMC article.
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Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study.
Coratti G, Bovis F, Pera MC, Scoto M, Montes J, Pasternak A, Mayhew A, Muni-Lofra R, Duong T, Rohwer A, Dunaway Young S, Civitello M, Salmin F, Mizzoni I, Morando S, Pane M, Albamonte E, D'Amico A, Brolatti N, Sframeli M, Marini-Bettolo C, Sansone VA, Bruno C, Messina S, Bertini E, Baranello G, Day J, Darras BT, De Vivo DC, Hirano M, Muntoni F, Finkel R, Mercuri E; ISMAC group.
Coratti G, et al.
Eur J Neurol. 2024 Apr 24:e16309. doi: 10.1111/ene.16309. Online ahead of print.
Eur J Neurol. 2024.
PMID: 38656662
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