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Leveraging gene therapy to achieve long-term continuous or controllable expression of biotherapeutics.
Sci Adv. 2022 Jul 15;8(28):eabm1890. doi: 10.1126/sciadv.abm1890. Epub 2022 Jul 13.
Sci Adv. 2022.
PMID: 35857488
Free PMC article.
Alternative RNA splicing defects in pediatric cancers: new insights in tumorigenesis and potential therapeutic vulnerabilities.
Venkataramany AS, Schieffer KM, Lee K, Cottrell CE, Wang PY, Mardis ER, Cripe TP, Chandler DS.
Venkataramany AS, et al.
Ann Oncol. 2022 Jun;33(6):578-592. doi: 10.1016/j.annonc.2022.03.011. Epub 2022 Mar 23.
Ann Oncol. 2022.
PMID: 35339647
Free article.
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