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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2012 | 2 |
2013 | 1 |
2014 | 2 |
2019 | 1 |
2020 | 1 |
2021 | 1 |
2024 | 0 |
Search Results
6 results
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Page 1
Gene delivery using AAV8 in vivo for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCID.
Mol Ther Methods Clin Dev. 2021 Feb 15;20:765-778. doi: 10.1016/j.omtm.2021.02.007. eCollection 2021 Mar 12.
Mol Ther Methods Clin Dev. 2021.
PMID: 33738330
Free PMC article.
Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice.
Carbonaro-Sarracino DA, Tarantal AF, Lee CCI, Kaufman ML, Wandro S, Jin X, Martinez M, Clark DN, Chun K, Koziol C, Hardee CL, Wang X, Kohn DB.
Carbonaro-Sarracino DA, et al.
Mol Ther Methods Clin Dev. 2019 Nov 16;16:78-93. doi: 10.1016/j.omtm.2019.11.004. eCollection 2020 Mar 13.
Mol Ther Methods Clin Dev. 2019.
PMID: 31871959
Free PMC article.
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Effects of vector backbone and pseudotype on lentiviral vector-mediated gene transfer: studies in infant ADA-deficient mice and rhesus monkeys.
Carbonaro Sarracino D, Tarantal AF, Lee CC, Martinez M, Jin X, Wang X, Hardee CL, Geiger S, Kahl CA, Kohn DB.
Carbonaro Sarracino D, et al.
Mol Ther. 2014 Oct;22(10):1803-16. doi: 10.1038/mt.2014.88. Epub 2014 Jun 13.
Mol Ther. 2014.
PMID: 24925206
Free PMC article.
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Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency.
Carbonaro DA, Zhang L, Jin X, Montiel-Equihua C, Geiger S, Carmo M, Cooper A, Fairbanks L, Kaufman ML, Sebire NJ, Hollis RP, Blundell MP, Senadheera S, Fu PY, Sahaghian A, Chan RY, Wang X, Cornetta K, Thrasher AJ, Kohn DB, Gaspar HB.
Carbonaro DA, et al.
Mol Ther. 2014 Mar;22(3):607-622. doi: 10.1038/mt.2013.265. Epub 2013 Nov 20.
Mol Ther. 2014.
PMID: 24256635
Free PMC article.
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Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreduction.
Carbonaro DA, Jin X, Wang X, Yu XJ, Rozengurt N, Kaufman ML, Wang X, Gjertson D, Zhou Y, Blackburn MR, Kohn DB.
Carbonaro DA, et al.
Blood. 2012 Nov 1;120(18):3677-87. doi: 10.1182/blood-2012-02-408591. Epub 2012 Jul 25.
Blood. 2012.
PMID: 22833548
Free PMC article.
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Nonmyeloablative conditioning regimen to increase engraftment of gene-modified hematopoietic stem cells in young rhesus monkeys.
Tarantal AF, Giannoni F, Lee CC, Wherley J, Sumiyoshi T, Martinez M, Kahl CA, Elashoff D, Louie SG, Kohn DB.
Tarantal AF, et al.
Mol Ther. 2012 May;20(5):1033-45. doi: 10.1038/mt.2011.312. Epub 2012 Jan 31.
Mol Ther. 2012.
PMID: 22294147
Free PMC article.
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