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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2022 | 1 |
2023 | 6 |
2024 | 0 |
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7 results
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Page 1
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTD.
bioRxiv [Preprint]. 2023 Dec 12:2023.12.12.571328. doi: 10.1101/2023.12.12.571328.
bioRxiv. 2023.
PMID: 38168370
Free PMC article.
Preprint.
Protein Engineering Technologies for Development of Next-Generation Genome Editors.
Winter J, Shirguppe S, Perez-Pinera P.
Winter J, et al.
Curr Opin Biomed Eng. 2023 Dec;28:100514. doi: 10.1016/j.cobme.2023.100514. Epub 2023 Nov 1.
Curr Opin Biomed Eng. 2023.
PMID: 38095011
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Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins.
Zeballos C MA, Moore HJ, Smith TJ, Powell JE, Ahsan NS, Zhang S, Gaj T.
Zeballos C MA, et al.
Nat Commun. 2023 Oct 14;14(1):6492. doi: 10.1038/s41467-023-42147-z.
Nat Commun. 2023.
PMID: 37838698
Free PMC article.
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Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors.
Gapinske M, Winter J, Swami D, Gapinske L, Woods WS, Shirguppe S, Miskalis A, Busza A, Joulani D, Kao CJ, Kostan K, Bigot A, Bashir R, Perez-Pinera P.
Gapinske M, et al.
Mol Ther Nucleic Acids. 2023 Jul 27;33:572-586. doi: 10.1016/j.omtn.2023.07.029. eCollection 2023 Sep 12.
Mol Ther Nucleic Acids. 2023.
PMID: 37637209
Free PMC article.
Item in Clipboard
Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins.
Zeballos C MA, Moore HJ, Smith TJ, Powell JE, Ahsan NS, Zhang S, Gaj T.
Zeballos C MA, et al.
bioRxiv [Preprint]. 2023 Aug 26:2023.04.07.536072. doi: 10.1101/2023.04.07.536072.
bioRxiv. 2023.
PMID: 37066174
Free PMC article.
Updated.
Preprint.
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Delivering Base Editors In Vivo by Adeno-Associated Virus Vectors.
Lim CKW, Miskalis AJ, Perez-Pinera P, Gaj T.
Lim CKW, et al.
Methods Mol Biol. 2023;2606:135-158. doi: 10.1007/978-1-0716-2879-9_11.
Methods Mol Biol. 2023.
PMID: 36592313
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CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes.
Lim CKW, McCallister TX, Saporito-Magriña C, McPheron GD, Krishnan R, Zeballos C MA, Powell JE, Clark LV, Perez-Pinera P, Gaj T.
Lim CKW, et al.
Mol Ther. 2022 Dec 7;30(12):3619-3631. doi: 10.1016/j.ymthe.2022.08.008. Epub 2022 Aug 13.
Mol Ther. 2022.
PMID: 35965414
Free PMC article.
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