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Erratum: Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model.
Zancanella V, Vallès A, Liefhebber JMP, Paerels L, Tornero CV, Wattimury H, van der Zon T, van Rooijen K, Golinska M, Grevelink T, Ehlert E, Pieterman EJ, Keijzer N, Gerardus Princen HM, Stokman G, Liu YP. Zancanella V, et al. Among authors: paerels l. Mol Ther Nucleic Acids. 2024 Apr 18;35(2):102189. doi: 10.1016/j.omtn.2024.102189. eCollection 2024 Jun 11. Mol Ther Nucleic Acids. 2024. PMID: 38681817 Free PMC article.
Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model.
Zancanella V, Vallès A, Liefhebber JMP, Paerels L, Tornero CV, Wattimury H, van der Zon T, van Rooijen K, Golinska M, Grevelink T, Ehlert E, Pieterman EJ, Keijzer N, Princen HMG, Stokman G, Liu YP. Zancanella V, et al. Among authors: paerels l. Mol Ther Nucleic Acids. 2023 Apr 7;32:454-467. doi: 10.1016/j.omtn.2023.04.004. eCollection 2023 Jun 13. Mol Ther Nucleic Acids. 2023. PMID: 37168797 Free PMC article.
Widespread and sustained target engagement in Huntington's disease minipigs upon intrastriatal microRNA-based gene therapy.
Vallès A, Evers MM, Stam A, Sogorb-Gonzalez M, Brouwers C, Vendrell-Tornero C, Acar-Broekmans S, Paerels L, Klima J, Bohuslavova B, Pintauro R, Fodale V, Bresciani A, Liscak R, Urgosik D, Starek Z, Crha M, Blits B, Petry H, Ellederova Z, Motlik J, van Deventer S, Konstantinova P. Vallès A, et al. Among authors: paerels l. Sci Transl Med. 2021 Apr 7;13(588):eabb8920. doi: 10.1126/scitranslmed.abb8920. Sci Transl Med. 2021. PMID: 33827977