Treatment of refractory/relapsed Diamond-Blackfan anaemia with eltrombopag.
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Br J Haematol. 2024 May;204(5):2077-2085. doi: 10.1111/bjh.19357. Epub 2024 Mar 10.
Br J Haematol. 2024.
PMID: 38462764
Clinical Trial.