Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My NCBI Filters

Text availability

Article attribute

Article type

Publication date

Search Results

15 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Results By Year timeline is not available.
Page 1
Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model.
Zancanella V, Vallès A, Liefhebber JMP, Paerels L, Tornero CV, Wattimury H, van der Zon T, van Rooijen K, Golinska M, Grevelink T, Ehlert E, Pieterman EJ, Keijzer N, Princen HMG, Stokman G, Liu YP. Zancanella V, et al. Among authors: liefhebber jmp. Mol Ther Nucleic Acids. 2023 Apr 7;32:454-467. doi: 10.1016/j.omtn.2023.04.004. eCollection 2023 Jun 13. Mol Ther Nucleic Acids. 2023. PMID: 37168797 Free PMC article.
Targeting RNA-Mediated Toxicity in C9orf72 ALS and/or FTD by RNAi-Based Gene Therapy.
Martier R, Liefhebber JM, García-Osta A, Miniarikova J, Cuadrado-Tejedor M, Espelosin M, Ursua S, Petry H, van Deventer SJ, Evers MM, Konstantinova P. Martier R, et al. Mol Ther Nucleic Acids. 2019 Jun 7;16:26-37. doi: 10.1016/j.omtn.2019.02.001. Epub 2019 Feb 11. Mol Ther Nucleic Acids. 2019. PMID: 30825670 Free PMC article.
Erratum: Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model.
Zancanella V, Vallès A, Liefhebber JMP, Paerels L, Tornero CV, Wattimury H, van der Zon T, van Rooijen K, Golinska M, Grevelink T, Ehlert E, Pieterman EJ, Keijzer N, Gerardus Princen HM, Stokman G, Liu YP. Zancanella V, et al. Among authors: liefhebber jmp. Mol Ther Nucleic Acids. 2024 Apr 18;35(2):102189. doi: 10.1016/j.omtn.2024.102189. eCollection 2024 Jun 11. Mol Ther Nucleic Acids. 2024. PMID: 38681817 Free PMC article.
15 results