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Page 1
Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.
Ponder KP, O'Malley TM, Wang P, O'Donnell PA, Traas AM, Knox VW, Aguirre GA, Ellinwood NM, Metcalf JA, Wang B, Parkinson-Lawrence EJ, Sleeper MM, Brooks DA, Hopwood JJ, Haskins ME. Ponder KP, et al. Among authors: knox vw. Mol Ther. 2012 May;20(5):898-907. doi: 10.1038/mt.2012.9. Epub 2012 Mar 6. Mol Ther. 2012. PMID: 22395531 Free PMC article.
Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs.
Ponder KP, Melniczek JR, Xu L, Weil MA, O'Malley TM, O'Donnell PA, Knox VW, Aguirre GD, Mazrier H, Ellinwood NM, Sleeper M, Maguire AM, Volk SW, Mango RL, Zweigle J, Wolfe JH, Haskins ME. Ponder KP, et al. Among authors: knox vw. Proc Natl Acad Sci U S A. 2002 Oct 1;99(20):13102-7. doi: 10.1073/pnas.192353499. Epub 2002 Sep 13. Proc Natl Acad Sci U S A. 2002. PMID: 12232044 Free PMC article.
Long-term amelioration of feline Mucopolysaccharidosis VI after AAV-mediated liver gene transfer.
Cotugno G, Annunziata P, Tessitore A, O'Malley T, Capalbo A, Faella A, Bartolomeo R, O'Donnell P, Wang P, Russo F, Sleeper MM, Knox VW, Fernandez S, Levanduski L, Hopwood J, De Leonibus E, Haskins M, Auricchio A. Cotugno G, et al. Among authors: knox vw. Mol Ther. 2011 Mar;19(3):461-9. doi: 10.1038/mt.2010.257. Epub 2010 Nov 30. Mol Ther. 2011. PMID: 21119624 Free PMC article.
Pharmacodynamics, pharmacokinetics and biodistribution of recombinant human N-acetylgalactosamine 4-sulfatase after 6months of therapy in cats using different IV infusion durations.
Ruane T, Haskins M, Cheng A, Wang P, Aguirre G, Knox VW 4th, Qi Y, Tompkins T, O'Neill CA. Ruane T, et al. Among authors: knox vw 4th. Mol Genet Metab. 2016 Feb;117(2):157-63. doi: 10.1016/j.ymgme.2015.10.006. Epub 2015 Oct 21. Mol Genet Metab. 2016. PMID: 26776148 Free article.
Bone marrow transplantation for feline mucopolysaccharidosis I.
Ellinwood NM, Colle MA, Weil MA, Casal ML, Vite CH, Wiemelt S, Hasson CW, O'Malley TM, He X, Prociuk U, Verot L, Melniczek JR, Lannon A, Aguirre GD, Knox VW, Evans SM, Vanier MT, Schuchman EH, Walkley SU, Haskins ME. Ellinwood NM, et al. Among authors: knox vw. Mol Genet Metab. 2007 Jul;91(3):239-50. doi: 10.1016/j.ymgme.2007.03.001. Epub 2007 May 7. Mol Genet Metab. 2007. PMID: 17482862 Free PMC article.
12 results