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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2008 | 1 |
2009 | 1 |
2010 | 1 |
2011 | 3 |
2013 | 1 |
2014 | 1 |
2024 | 0 |
Search Results
7 results
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Page 1
Long-term safety and efficacy of factor IX gene therapy in hemophilia B.
N Engl J Med. 2014 Nov 20;371(21):1994-2004. doi: 10.1056/NEJMoa1407309.
N Engl J Med. 2014.
PMID: 25409372
Free PMC article.
Clinical Trial.
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.
McIntosh J, Lenting PJ, Rosales C, Lee D, Rabbanian S, Raj D, Patel N, Tuddenham EG, Christophe OD, McVey JH, Waddington S, Nienhuis AW, Gray JT, Fagone P, Mingozzi F, Zhou SZ, High KA, Cancio M, Ng CY, Zhou J, Morton CL, Davidoff AM, Nathwani AC.
McIntosh J, et al.
Blood. 2013 Apr 25;121(17):3335-44. doi: 10.1182/blood-2012-10-462200. Epub 2013 Feb 20.
Blood. 2013.
PMID: 23426947
Free PMC article.
Item in Clipboard
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.
Nathwani AC, Tuddenham EG, Rangarajan S, Rosales C, McIntosh J, Linch DC, Chowdary P, Riddell A, Pie AJ, Harrington C, O'Beirne J, Smith K, Pasi J, Glader B, Rustagi P, Ng CY, Kay MA, Zhou J, Spence Y, Morton CL, Allay J, Coleman J, Sleep S, Cunningham JM, Srivastava D, Basner-Tschakarjan E, Mingozzi F, High KA, Gray JT, Reiss UM, Nienhuis AW, Davidoff AM.
Nathwani AC, et al.
N Engl J Med. 2011 Dec 22;365(25):2357-65. doi: 10.1056/NEJMoa1108046. Epub 2011 Dec 10.
N Engl J Med. 2011.
PMID: 22149959
Free PMC article.
Clinical Trial.
Item in Clipboard
Self-complementary adeno-associated viral vectors for gene therapy of hemophilia B: progress and challenges.
Raj D, Davidoff AM, Nathwani AC.
Raj D, et al.
Expert Rev Hematol. 2011 Oct;4(5):539-49. doi: 10.1586/ehm.11.48.
Expert Rev Hematol. 2011.
PMID: 21939421
Free PMC article.
Review.
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Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.
Nathwani AC, Rosales C, McIntosh J, Rastegarlari G, Nathwani D, Raj D, Nawathe S, Waddington SN, Bronson R, Jackson S, Donahue RE, High KA, Mingozzi F, Ng CY, Zhou J, Spence Y, McCarville MB, Valentine M, Allay J, Coleman J, Sleep S, Gray JT, Nienhuis AW, Davidoff AM.
Nathwani AC, et al.
Mol Ther. 2011 May;19(5):876-85. doi: 10.1038/mt.2010.274. Epub 2011 Jan 18.
Mol Ther. 2011.
PMID: 21245849
Free PMC article.
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Targeting multiple angiogenic pathways for the treatment of neuroblastoma.
Williams RF, Myers AL, Sims TL, Ng CY, Nathwani AC, Davidoff AM.
Williams RF, et al.
J Pediatr Surg. 2010 Jun;45(6):1103-9. doi: 10.1016/j.jpedsurg.2010.02.073.
J Pediatr Surg. 2010.
PMID: 20620303
Free PMC article.
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Enhancing transduction of the liver by adeno-associated viral vectors.
Nathwani AC, Cochrane M, McIntosh J, Ng CY, Zhou J, Gray JT, Davidoff AM.
Nathwani AC, et al.
Gene Ther. 2009 Jan;16(1):60-9. doi: 10.1038/gt.2008.137. Epub 2008 Aug 14.
Gene Ther. 2009.
PMID: 18701909
Free PMC article.
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