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What Can RNA-Based Therapy Do for Monogenic Diseases?
Pharmaceutics. 2023 Jan 12;15(1):260. doi: 10.3390/pharmaceutics15010260.
Pharmaceutics. 2023.
PMID: 36678889
Free PMC article.
Review.
CFTR, Cell Junctions and the Cytoskeleton.
Pankonien I, Quaresma MC, Rodrigues CS, Amaral MD.
Pankonien I, et al.
Int J Mol Sci. 2022 Feb 28;23(5):2688. doi: 10.3390/ijms23052688.
Int J Mol Sci. 2022.
PMID: 35269829
Free PMC article.
Review.
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