Search Page
Save citations to file
Email citations
Send citations to clipboard
Add to Collections
Add to My Bibliography
Create a file for external citation management software
Your saved search
Your RSS Feed
Search Results
8 results
Filters applied: . Clear all
Results are displayed in a computed author sort order.
The Results By Year timeline is not available.
Page 1
Effects of vector backbone and pseudotype on lentiviral vector-mediated gene transfer: studies in infant ADA-deficient mice and rhesus monkeys.
Mol Ther. 2014 Oct;22(10):1803-16. doi: 10.1038/mt.2014.88. Epub 2014 Jun 13.
Mol Ther. 2014.
PMID: 24925206
Free PMC article.
Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice.
Carbonaro-Sarracino DA, Tarantal AF, Lee CCI, Kaufman ML, Wandro S, Jin X, Martinez M, Clark DN, Chun K, Koziol C, Hardee CL, Wang X, Kohn DB.
Carbonaro-Sarracino DA, et al.
Mol Ther Methods Clin Dev. 2019 Nov 16;16:78-93. doi: 10.1016/j.omtm.2019.11.004. eCollection 2020 Mar 13.
Mol Ther Methods Clin Dev. 2019.
PMID: 31871959
Free PMC article.
Item in Clipboard
Gene delivery using AAV8 in vivo for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCID.
Carbonaro-Sarracino DA, Chun K, Clark DN, Kaufman ML, Jin X, Wang X, Kohn DB.
Carbonaro-Sarracino DA, et al.
Mol Ther Methods Clin Dev. 2021 Feb 15;20:765-778. doi: 10.1016/j.omtm.2021.02.007. eCollection 2021 Mar 12.
Mol Ther Methods Clin Dev. 2021.
PMID: 33738330
Free PMC article.
Item in Clipboard
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients.
Cooper AR, Lill GR, Shaw K, Carbonaro-Sarracino DA, Davila A, Sokolic R, Candotti F, Pellegrini M, Kohn DB.
Cooper AR, et al. Among authors: carbonaro sarracino da.
Blood. 2017 May 11;129(19):2624-2635. doi: 10.1182/blood-2016-12-756734. Epub 2017 Mar 28.
Blood. 2017.
PMID: 28351939
Free PMC article.
Clinical Trial.
Item in Clipboard
Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID): Molecular Pathogenesis and Clinical Manifestations.
Bradford KL, Moretti FA, Carbonaro-Sarracino DA, Gaspar HB, Kohn DB.
Bradford KL, et al. Among authors: carbonaro sarracino da.
J Clin Immunol. 2017 Oct;37(7):626-637. doi: 10.1007/s10875-017-0433-3. Epub 2017 Aug 25.
J Clin Immunol. 2017.
PMID: 28842866
Review.
Item in Clipboard
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency.
Reinhardt B, Habib O, Shaw KL, Garabedian E, Carbonaro-Sarracino DA, Terrazas D, Fernandez BC, De Oliveira S, Moore TB, Ikeda AK, Engel BC, Podsakoff GM, Hollis RP, Fernandes A, Jackson C, Shupien S, Mishra S, Davila A, Mottahedeh J, Vitomirov A, Meng W, Rosenfeld AM, Roche AM, Hokama P, Reddy S, Everett J, Wang X, Luning Prak ET, Cornetta K, Hershfield MS, Sokolic R, De Ravin SS, Malech HL, Bushman FD, Candotti F, Kohn DB.
Reinhardt B, et al. Among authors: carbonaro sarracino da.
Blood. 2021 Oct 14;138(15):1304-1316. doi: 10.1182/blood.2020010260.
Blood. 2021.
PMID: 33974038
Free PMC article.
Clinical Trial.
Item in Clipboard
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
Kohn DB, Booth C, Shaw KL, Xu-Bayford J, Garabedian E, Trevisan V, Carbonaro-Sarracino DA, Soni K, Terrazas D, Snell K, Ikeda A, Leon-Rico D, Moore TB, Buckland KF, Shah AJ, Gilmour KC, De Oliveira S, Rivat C, Crooks GM, Izotova N, Tse J, Adams S, Shupien S, Ricketts H, Davila A, Uzowuru C, Icreverzi A, Barman P, Campo Fernandez B, Hollis RP, Coronel M, Yu A, Chun KM, Casas CE, Zhang R, Arduini S, Lynn F, Kudari M, Spezzi A, Zahn M, Heimke R, Labik I, Parrott R, Buckley RH, Reeves L, Cornetta K, Sokolic R, Hershfield M, Schmidt M, Candotti F, Malech HL, Thrasher AJ, Gaspar HB.
Kohn DB, et al. Among authors: carbonaro sarracino da.
N Engl J Med. 2021 May 27;384(21):2002-2013. doi: 10.1056/NEJMoa2027675. Epub 2021 May 11.
N Engl J Med. 2021.
PMID: 33974366
Free PMC article.
Clinical Trial.
Item in Clipboard
Letter to the Editor. Differences between lentiviral vector-mediated ex vivo hematopoietic stem cell and adeno-associated virus gene therapies for neurological disorders.
Carbonaro-Sarracino DA, LeWinter R, Meltzer L.
Carbonaro-Sarracino DA, et al.
J Neurosurg. 2021 Dec 10;136(5):1501. doi: 10.3171/2021.10.JNS212456.
J Neurosurg. 2021.
PMID: 34891135
No abstract available.
Item in Clipboard
Cite
Cite