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Precision Medicine for Lysosomal Disorders.
Biomolecules. 2020 Jul 26;10(8):1110. doi: 10.3390/biom10081110.
Biomolecules. 2020.
PMID: 32722587
Free PMC article.
Review.
Estimated birth prevalence of mucopolysaccharidoses in Brazil.
Federhen A, Pasqualim G, de Freitas TF, Gonzalez EA, Trapp F, Matte U, Giugliani R.
Federhen A, et al.
Am J Med Genet A. 2020 Mar;182(3):469-483. doi: 10.1002/ajmg.a.61456. Epub 2020 Jan 11.
Am J Med Genet A. 2020.
PMID: 31926052
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