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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2012 | 1 |
2013 | 1 |
2016 | 2 |
2017 | 2 |
2019 | 1 |
2024 | 0 |
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Page 1
Small Molecules in Development for the Treatment of Spinal Muscular Atrophy.
J Med Chem. 2016 Nov 23;59(22):10067-10083. doi: 10.1021/acs.jmedchem.6b00670. Epub 2016 Aug 16.
J Med Chem. 2016.
PMID: 27490705
Free PMC article.
Review.
ML372 blocks SMN ubiquitination and improves spinal muscular atrophy pathology in mice.
Abera MB, Xiao J, Nofziger J, Titus S, Southall N, Zheng W, Moritz KE, Ferrer M, Cherry JJ, Androphy EJ, Wang A, Xu X, Austin C, Fischbeck KH, Marugan JJ, Burnett BG.
Abera MB, et al.
JCI Insight. 2016 Nov 17;1(19):e88427. doi: 10.1172/jci.insight.88427.
JCI Insight. 2016.
PMID: 27882347
Free PMC article.
Item in Clipboard
Discovery of a Small Molecule Probe That Post-Translationally Stabilizes the Survival Motor Neuron Protein for the Treatment of Spinal Muscular Atrophy.
Rietz A, Li H, Quist KM, Cherry JJ, Lorson CL, Burnett BG, Kern NL, Calder AN, Fritsche M, Lusic H, Boaler PJ, Choi S, Xing X, Glicksman MA, Cuny GD, Androphy EJ, Hodgetts KJ.
Rietz A, et al.
J Med Chem. 2017 Jun 8;60(11):4594-4610. doi: 10.1021/acs.jmedchem.6b01885. Epub 2017 May 19.
J Med Chem. 2017.
PMID: 28481536
Free PMC article.
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Optimization of a series of heterocycles as survival motor neuron gene transcription enhancers.
Choi S, Calder AN, Miller EH, Anderson KP, Fiejtek DK, Rietz A, Li H, Cherry JJ, Quist KM, Xing X, Glicksman MA, Cuny GD, Lorson CL, Androphy EA, Hodgetts KJ.
Choi S, et al.
Bioorg Med Chem Lett. 2017 Dec 1;27(23):5144-5148. doi: 10.1016/j.bmcl.2017.10.066. Epub 2017 Oct 26.
Bioorg Med Chem Lett. 2017.
PMID: 29103974
Free PMC article.
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Intraperitoneal delivery of a novel drug-like compound improves disease severity in severe and intermediate mouse models of Spinal Muscular Atrophy.
Osman EY, Rietz A, Kline RA, Cherry JJ, Hodgetts KJ, Lorson CL, Androphy EJ.
Osman EY, et al.
Sci Rep. 2019 Feb 7;9(1):1633. doi: 10.1038/s41598-018-38208-9.
Sci Rep. 2019.
PMID: 30733501
Free PMC article.
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Enhancement of SMN protein levels in a mouse model of spinal muscular atrophy using novel drug-like compounds.
Cherry JJ, Osman EY, Evans MC, Choi S, Xing X, Cuny GD, Glicksman MA, Lorson CL, Androphy EJ.
Cherry JJ, et al.
EMBO Mol Med. 2013 Jul;5(7):1103-18. doi: 10.1002/emmm.201202305. Epub 2013 Jun 5.
EMBO Mol Med. 2013.
PMID: 23740718
Free PMC article.
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Identification of novel compounds that increase SMN protein levels using an improved SMN2 reporter cell assay.
Cherry JJ, Evans MC, Ni J, Cuny GD, Glicksman MA, Androphy EJ.
Cherry JJ, et al.
J Biomol Screen. 2012 Apr;17(4):481-95. doi: 10.1177/1087057111431605. Epub 2012 Jan 10.
J Biomol Screen. 2012.
PMID: 22233647
Free PMC article.
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