R01 NS088766/NS/NINDS NIH HHS/United States[Grants and Funding] - Search Results

Year	Number of Results
2016	1
2018	1
2020	2
2021	5
2024	0

1

Mucopolysaccharidoses type I gene therapy.

Hurt SC, Dickson PI, Curiel DT. Hurt SC, et al. J Inherit Metab Dis. 2021 Sep;44(5):1088-1098. doi: 10.1002/jimd.12414. Epub 2021 Jul 9. J Inherit Metab Dis. 2021. PMID: 34189746 Free PMC article. Review.

2

Neuropathology of murine Sanfilippo D syndrome.

Takahashi K, Le SQ, Kan SH, Jansen MJ, Dickson PI, Cooper JD. Takahashi K, et al. Mol Genet Metab. 2021 Dec;134(4):323-329. doi: 10.1016/j.ymgme.2021.11.010. Epub 2021 Nov 24. Mol Genet Metab. 2021. PMID: 34844863

3

Temporospatial Development of Neuropathologic Findings in a Canine Model of Mucopolysaccharidosis IIIB.

Harm TA, Hostetter SJ, Nenninger AS, Valentine BN, Ellinwood NM, Smith JD. Harm TA, et al. Vet Pathol. 2021 Jan;58(1):205-222. doi: 10.1177/0300985820960128. Epub 2020 Nov 18. Vet Pathol. 2021. PMID: 33205707 Free PMC article.

4

Enzyme Replacement Therapy for Mucopolysaccharidosis IIID using Recombinant Human α-N-Acetylglucosamine-6-Sulfatase in Neonatal Mice.

Wang F, Moen DR, Sauni C, Kan SH, Li S, Le SQ, Lomenick B, Zhang X, Ekins S, Singamsetty S, Wood J, Dickson PI, Chou TF. Wang F, et al. Mol Pharm. 2021 Jan 4;18(1):214-227. doi: 10.1021/acs.molpharmaceut.0c00831. Epub 2020 Dec 15. Mol Pharm. 2021. PMID: 33320673 Free PMC article.

5

Biochemical evaluation of intracerebroventricular rhNAGLU-IGF2 enzyme replacement therapy in neonatal mice with Sanfilippo B syndrome.

Kan SH, Elsharkawi I, Le SQ, Prill H, Mangini L, Cooper JD, Lawrence R, Sands MS, Crawford BE, Dickson PI. Kan SH, et al. Mol Genet Metab. 2021 Jun;133(2):185-192. doi: 10.1016/j.ymgme.2021.03.013. Epub 2021 Mar 31. Mol Genet Metab. 2021. PMID: 33839004 Free PMC article.

6

Behavioral deficits and cholinergic pathway abnormalities in male Sanfilippo B mice.

Kan SH, Le SQ, Bui QD, Benedict B, Cushman J, Sands MS, Dickson PI. Kan SH, et al. Behav Brain Res. 2016 Oct 1;312:265-71. doi: 10.1016/j.bbr.2016.06.023. Epub 2016 Jun 23. Behav Brain Res. 2016. PMID: 27340089 Free PMC article.

7

Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice.

Clarke D, Pearse Y, Kan SH, Le SQ, Sanghez V, Cooper JD, Dickson PI, Iacovino M. Clarke D, et al. Mol Ther Methods Clin Dev. 2018 Jul 23;10:113-127. doi: 10.1016/j.omtm.2018.06.005. eCollection 2018 Sep 21. Mol Ther Methods Clin Dev. 2018. PMID: 30101150 Free PMC article.

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