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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2014 | 1 |
2020 | 1 |
2021 | 2 |
2022 | 3 |
2024 | 0 |
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6 results
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Page 1
Risdiplam in Type 1 Spinal Muscular Atrophy.
N Engl J Med. 2021 Mar 11;384(10):915-923. doi: 10.1056/NEJMoa2009965. Epub 2021 Feb 24.
N Engl J Med. 2021.
PMID: 33626251
Clinical Trial.
Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls.
Darras BT, Masson R, Mazurkiewicz-Bełdzińska M, Rose K, Xiong H, Zanoteli E, Baranello G, Bruno C, Vlodavets D, Wang Y, El-Khairi M, Gerber M, Gorni K, Khwaja O, Kletzl H, Scalco RS, Fontoura P, Servais L; FIREFISH Working Group.
Darras BT, et al.
N Engl J Med. 2021 Jul 29;385(5):427-435. doi: 10.1056/NEJMoa2102047.
N Engl J Med. 2021.
PMID: 34320287
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Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial.
Masson R, Mazurkiewicz-Bełdzińska M, Rose K, Servais L, Xiong H, Zanoteli E, Baranello G, Bruno C, Day JW, Deconinck N, Klein A, Mercuri E, Vlodavets D, Wang Y, Dodman A, El-Khairi M, Gorni K, Jaber B, Kletzl H, Gaki E, Fontoura P, Darras BT; FIREFISH Study Group.
Masson R, et al.
Lancet Neurol. 2022 Dec;21(12):1110-1119. doi: 10.1016/S1474-4422(22)00339-8. Epub 2022 Oct 14.
Lancet Neurol. 2022.
PMID: 36244364
Clinical Trial.
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Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial.
Mercuri E, Deconinck N, Mazzone ES, Nascimento A, Oskoui M, Saito K, Vuillerot C, Baranello G, Boespflug-Tanguy O, Goemans N, Kirschner J, Kostera-Pruszczyk A, Servais L, Gerber M, Gorni K, Khwaja O, Kletzl H, Scalco RS, Staunton H, Yeung WY, Martin C, Fontoura P, Day JW; SUNFISH Study Group.
Mercuri E, et al.
Lancet Neurol. 2022 Jan;21(1):42-52. doi: 10.1016/S1474-4422(21)00367-7.
Lancet Neurol. 2022.
PMID: 34942136
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Assessment of patient burden from dry eye disease using a combination of five visual analogue scales and a radar graph: a pilot study of the PENTASCORE.
Labetoulle M, Benichou J, M'nafek N, Garnier F, Rabut G, Ben Hadj Salah W, Labbé A, Rousseau A, Baudouin C.
Labetoulle M, et al.
Br J Ophthalmol. 2022 Apr;106(4):467-473. doi: 10.1136/bjophthalmol-2020-317473. Epub 2020 Dec 16.
Br J Ophthalmol. 2022.
PMID: 33328188
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[Induced astigmatism after corneal suture removal after cataract surgery].
Loriaut P, Kaswin G, Rousseau A, Meziani L, M'nafek N, Pogorzalek N, Labetoulle M.
Loriaut P, et al.
J Fr Ophtalmol. 2014 Mar;37(3):226-30. doi: 10.1016/j.jfo.2013.09.005. Epub 2014 Feb 18.
J Fr Ophtalmol. 2014.
PMID: 24559514
French.
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