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Efficacy and safety of compassionate use for rare diseases: a scoping review from 1991 to 2022.
Orphanet J Rare Dis. 2023 Nov 28;18(1):368. doi: 10.1186/s13023-023-02978-x.
Orphanet J Rare Dis. 2023.
PMID: 38017575
Free PMC article.
Review.
Facial onset sensory and motor neuronopathy (FOSMN syndrome): Cases series and systematic review.
Hu N, Zhang L, Yang X, Fu H, Cui L, Liu M.
Hu N, et al.
Neurol Sci. 2023 Jun;44(6):1969-1978. doi: 10.1007/s10072-023-06703-1. Epub 2023 Mar 3.
Neurol Sci. 2023.
PMID: 36864244
Review.
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