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Year Number of Results
2009 1
2011 1
2015 1
2016 2
2017 4
2019 1
2020 3
2021 8
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2023 2
2024 2

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Page 1
Development of a Thalassemia International Prognostic Scoring System (TIPSS).
Vitrano A, Musallam KM, Meloni A, Karimi M, Daar S, Ricchi P, Costantini S, Vlachaki E, Di Marco V, El-Beshlawy A, Hajipour M, Ansari SH, Filosa A, Ceci A, Singer ST, Naserullah ZA, Pepe A, Cademartiri F, Pollina SA, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A; International Working Group on Thalassemia (IWG-THAL). Vitrano A, et al. Among authors: bonifazi f. Blood Cells Mol Dis. 2023 Mar;99:102710. doi: 10.1016/j.bcmd.2022.102710. Epub 2022 Nov 25. Blood Cells Mol Dis. 2023. PMID: 36463683 Review.
Medical Device Development for Children and Young People-Reviewing the Challenges and Opportunities.
Dimitri P, Pignataro V, Lupo M, Bonifazi D, Henke M, Musazzi UM, Ernst F, Minghetti P, Redaelli DF, Antimisiaris SG, Migliaccio G, Bonifazi F, Marciani L, Courtenay AJ, Denora N, Lopedota A. Dimitri P, et al. Among authors: bonifazi f. Pharmaceutics. 2021 Dec 17;13(12):2178. doi: 10.3390/pharmaceutics13122178. Pharmaceutics. 2021. PMID: 34959459 Free PMC article. Review.
The ethical framework for performing research with rare inherited neurometabolic disease patients.
Giannuzzi V, Devlieger H, Margari L, Odlind VL, Ragab L, Bellettato CM, D'Avanzo F, Lampe C, Cassis L, Cortès-Saladelafont E, Cazorla ÁG, Barić I, Cvitanović-Šojat L, Fumić K, Dali CI, Bartoloni F, Bonifazi F, Scarpa M, Ceci A. Giannuzzi V, et al. Among authors: bonifazi f. Eur J Pediatr. 2017 Mar;176(3):395-405. doi: 10.1007/s00431-017-2852-9. Epub 2017 Jan 16. Eur J Pediatr. 2017. PMID: 28093642 Free PMC article. Review.
Risk of mortality from anemia and iron overload in nontransfusion-dependent β-thalassemia.
Musallam KM, Vitrano A, Meloni A, Pollina SA, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Ansari SH, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A; International Working Group on Thalassemia (IWG-THAL). Musallam KM, et al. Among authors: bonifazi f. Am J Hematol. 2022 Feb 1;97(2):E78-E80. doi: 10.1002/ajh.26428. Epub 2021 Dec 10. Am J Hematol. 2022. PMID: 34862982 Free article. No abstract available.
Review and evaluation of the methodological quality of the existing guidelines and recommendations for inherited neurometabolic disorders.
Cassis L, Cortès-Saladelafont E, Molero-Luis M, Yubero D, González MJ, Ormazábal A, Fons C, Jou C, Sierra C, Castejon Ponce E, Ramos F, Armstrong J, O'Callaghan MM, Casado M, Montero R, Meavilla-Olivas S, Artuch R, Barić I, Bartoloni F, Bellettato CM, Bonifazi F, Ceci A, Cvitanović-Šojat L, Dali CI, D'Avanzo F, Fumic K, Giannuzzi V, Lampe C, Scarpa M, Garcia-Cazorla Á. Cassis L, et al. Among authors: bonifazi f. Orphanet J Rare Dis. 2015 Dec 30;10:164. doi: 10.1186/s13023-015-0376-9. Orphanet J Rare Dis. 2015. PMID: 26714856 Free PMC article. Review.
Iron chelation therapy in thalassemia major: a systematic review with meta-analyses of 1520 patients included on randomized clinical trials.
Maggio A, Filosa A, Vitrano A, Aloj G, Kattamis A, Ceci A, Fucharoen S, Cianciulli P, Grady RW, Prossomariti L, Porter JB, Iacono A, Cappellini MD, Bonifazi F, Cassarà F, Harmatz P, Wood J, Gluud C. Maggio A, et al. Among authors: bonifazi f. Blood Cells Mol Dis. 2011 Oct 15;47(3):166-75. doi: 10.1016/j.bcmd.2011.07.002. Epub 2011 Aug 16. Blood Cells Mol Dis. 2011. PMID: 21843958 Review.
Survival and causes of death in 2,033 patients with non-transfusion-dependent β-thalassemia.
Musallam KM, Vitrano A, Meloni A, Pollina SA, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Ansari SH, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A. Musallam KM, et al. Among authors: bonifazi f. Haematologica. 2021 Sep 1;106(9):2489-2492. doi: 10.3324/haematol.2021.278684. Haematologica. 2021. PMID: 33882642 Free PMC article. No abstract available.
25 results