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2017 1
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2023 4
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Page 1
Transcriptome-Guided Drug Repurposing for Aggressive SCCs.
Zauner R, Wimmer M, Dorfer S, Ablinger M, Koller U, Piñón Hofbauer J, Guttmann-Gruber C, Bauer JW, Wally V. Zauner R, et al. Among authors: guttmann gruber c. Int J Mol Sci. 2022 Jan 17;23(2):1007. doi: 10.3390/ijms23021007. Int J Mol Sci. 2022. PMID: 35055192 Free PMC article.
COL7A1 Editing via RNA Trans-Splicing in RDEB-Derived Skin Equivalents.
Liemberger B, Bischof J, Ablinger M, Hainzl S, Murauer EM, Lackner N, Ebner P, Kocher T, Nyström A, Wally V, Mayr E, Guttmann-Gruber C, Hofbauer JP, Bauer JW, Koller U. Liemberger B, et al. Among authors: guttmann gruber c. Int J Mol Sci. 2023 Feb 22;24(5):4341. doi: 10.3390/ijms24054341. Int J Mol Sci. 2023. PMID: 36901775 Free PMC article.
Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.
Bischof J, March OP, Liemberger B, Haas SA, Hainzl S, Petković I, Leb-Reichl V, Illmer J, Korotchenko E, Klausegger A, Hoog A, Binder HM, Garcia M, Duarte B, Strunk D, Larcher F, Reichelt J, Guttmann-Gruber C, Wally V, Hofbauer JP, Bauer JW, Cathomen T, Kocher T, Koller U. Bischof J, et al. Among authors: guttmann gruber c. Mol Ther. 2022 Aug 3;30(8):2680-2692. doi: 10.1016/j.ymthe.2022.04.020. Epub 2022 Apr 30. Mol Ther. 2022. PMID: 35490295 Free PMC article.
MicroRNA-200b-mediated reversion of a spectrum of epithelial-to-mesenchymal transition states in recessive dystrophic epidermolysis bullosa squamous cell carcinomas.
Illmer J, Zauner R, Piñón Hofbauer J, Wimmer M, Gruner S, Ablinger M, Bischof J, Dorfer S, Hainzl S, Tober V, Bergson S, Sarig O, Samuelov L, Guttmann-Gruber C, Shalom-Feuerstein R, Sprecher E, Koller U, Laimer M, Bauer JW, Wally V. Illmer J, et al. Among authors: guttmann gruber c. Br J Dermatol. 2023 Dec 20;190(1):80-93. doi: 10.1093/bjd/ljad335. Br J Dermatol. 2023. PMID: 37681509
Challenges and progress related to gene editing in rare skin diseases.
Piñón Hofbauer J, Guttmann-Gruber C, Wally V, Sharma A, Gratz IK, Koller U. Piñón Hofbauer J, et al. Among authors: guttmann gruber c. Adv Drug Deliv Rev. 2024 May;208:115294. doi: 10.1016/j.addr.2024.115294. Epub 2024 Mar 23. Adv Drug Deliv Rev. 2024. PMID: 38527624 Free article. Review.
COL17A1 editing via homology-directed repair in junctional epidermolysis bullosa.
Petković I, Bischof J, Kocher T, March OP, Liemberger B, Hainzl S, Strunk D, Raninger AM, Binder HM, Reichelt J, Guttmann-Gruber C, Wally V, Piñón Hofbauer J, Bauer JW, Koller U. Petković I, et al. Among authors: guttmann gruber c. Front Med (Lausanne). 2022 Aug 25;9:976604. doi: 10.3389/fmed.2022.976604. eCollection 2022. Front Med (Lausanne). 2022. PMID: 36091706 Free PMC article.
5'RNA Trans-Splicing Repair of COL7A1 Mutant Transcripts in Epidermolysis Bullosa.
Mayr E, Ablinger M, Lettner T, Murauer EM, Guttmann-Gruber C, Piñón Hofbauer J, Hainzl S, Kaiser M, Klausegger A, Bauer JW, Koller U, Wally V. Mayr E, et al. Among authors: guttmann gruber c. Int J Mol Sci. 2022 Feb 2;23(3):1732. doi: 10.3390/ijms23031732. Int J Mol Sci. 2022. PMID: 35163654 Free PMC article.
Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination.
Kocher T, Wagner RN, Klausegger A, Guttmann-Gruber C, Hainzl S, Bauer JW, Reichelt J, Koller U. Kocher T, et al. Among authors: guttmann gruber c. Mol Ther Nucleic Acids. 2019 Dec 6;18:496-507. doi: 10.1016/j.omtn.2019.09.011. Epub 2019 Sep 20. Mol Ther Nucleic Acids. 2019. PMID: 31670199 Free PMC article.
27 results