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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2006 1
2007 2
2008 1
2009 1
2010 2
2011 4
2012 2
2013 3
2014 1
2015 4
2016 3
2017 1
2018 7
2019 6
2020 9
2021 2
2023 3
2024 5

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53 results

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Page 1
Fetal gene therapy.
Waddington SN, Peranteau WH, Rahim AA, Boyle AK, Kurian MA, Gissen P, Chan JKY, David AL. Waddington SN, et al. Among authors: rahim aa. J Inherit Metab Dis. 2024 Jan;47(1):192-210. doi: 10.1002/jimd.12659. Epub 2023 Aug 7. J Inherit Metab Dis. 2024. PMID: 37470194 Review.
Special edition: The NCLs/Batten disease.
Rahim AA, Russell C, Mole SE. Rahim AA, et al. Biochim Biophys Acta Mol Basis Dis. 2020 Sep 1;1866(9):165824. doi: 10.1016/j.bbadis.2020.165824. Epub 2020 May 5. Biochim Biophys Acta Mol Basis Dis. 2020. PMID: 32387426 Free article. No abstract available.
Experimental gene therapies for the NCLs.
Liu W, Kleine-Holthaus SM, Herranz-Martin S, Aristorena M, Mole SE, Smith AJ, Ali RR, Rahim AA. Liu W, et al. Among authors: rahim aa. Biochim Biophys Acta Mol Basis Dis. 2020 Sep 1;1866(9):165772. doi: 10.1016/j.bbadis.2020.165772. Epub 2020 Mar 24. Biochim Biophys Acta Mol Basis Dis. 2020. PMID: 32220628 Free article. Review.
Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism.
Ng J, Barral S, De La Fuente Barrigon C, Lignani G, Erdem FA, Wallings R, Privolizzi R, Rossignoli G, Alrashidi H, Heasman S, Meyer E, Ngoh A, Pope S, Karda R, Perocheau D, Baruteau J, Suff N, Antinao Diaz J, Schorge S, Vowles J, Marshall LR, Cowley SA, Sucic S, Freissmuth M, Counsell JR, Wade-Martins R, Heales SJR, Rahim AA, Bencze M, Waddington SN, Kurian MA. Ng J, et al. Among authors: rahim aa. Sci Transl Med. 2021 May 19;13(594):eaaw1564. doi: 10.1126/scitranslmed.aaw1564. Sci Transl Med. 2021. PMID: 34011628 Free PMC article.
Perinatal gene transfer to the liver.
McKay TR, Rahim AA, Buckley SM, Ward NJ, Chan JK, Howe SJ, Waddington SN. McKay TR, et al. Among authors: rahim aa. Curr Pharm Des. 2011;17(24):2528-41. doi: 10.2174/138161211797247541. Curr Pharm Des. 2011. PMID: 21774770 Free PMC article. Review.
Perinatal systemic gene delivery using adeno-associated viral vectors.
Karda R, Buckley SM, Mattar CN, Ng J, Massaro G, Hughes MP, Kurian MA, Baruteau J, Gissen P, Chan JK, Bacchelli C, Waddington SN, Rahim AA. Karda R, et al. Among authors: rahim aa. Front Mol Neurosci. 2014 Nov 14;7:89. doi: 10.3389/fnmol.2014.00089. eCollection 2014. Front Mol Neurosci. 2014. PMID: 25452713 Free PMC article. Review.
The neuronal ceroid lipofuscinoses: Opportunities from model systems.
Faller KM, Gutierrez-Quintana R, Mohammed A, Rahim AA, Tuxworth RI, Wager K, Bond M. Faller KM, et al. Among authors: rahim aa. Biochim Biophys Acta. 2015 Oct;1852(10 Pt B):2267-78. doi: 10.1016/j.bbadis.2015.04.022. Epub 2015 Apr 29. Biochim Biophys Acta. 2015. PMID: 25937302 Free article. Review.
53 results