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LNP-mediated delivery of CRISPR RNP for wide-spread in vivo genome editing in mouse cornea.
J Control Release. 2022 Oct;350:401-413. doi: 10.1016/j.jconrel.2022.08.042. Epub 2022 Aug 27.
J Control Release. 2022.
PMID: 36029893
Free article.
ABE8e Corrects Pax6-Aniridic Variant in Humanized Mouse ESCs and via LNPs in Ex Vivo Cortical Neurons.
Adair BA, Korecki AJ, Djaksigulova D, Wagner PK, Chiu NY, Lam SL, Lengyell TC, Leavitt BR, Simpson EM.
Adair BA, et al. Among authors: djaksigulova d.
Ophthalmol Ther. 2023 Aug;12(4):2049-2068. doi: 10.1007/s40123-023-00729-6. Epub 2023 May 20.
Ophthalmol Ther. 2023.
PMID: 37210469
Free PMC article.
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