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Emerging therapies for Duchenne muscular dystrophy.
Markati T, Oskoui M, Farrar MA, Duong T, Goemans N, Servais L. Markati T, et al. Among authors: farrar ma. Lancet Neurol. 2022 Sep;21(9):814-829. doi: 10.1016/S1474-4422(22)00125-9. Epub 2022 Jul 15. Lancet Neurol. 2022. PMID: 35850122 Review.
Emerging therapies and challenges in spinal muscular atrophy.
Farrar MA, Park SB, Vucic S, Carey KA, Turner BJ, Gillingwater TH, Swoboda KJ, Kiernan MC. Farrar MA, et al. Ann Neurol. 2017 Mar;81(3):355-368. doi: 10.1002/ana.24864. Epub 2017 Feb 17. Ann Neurol. 2017. PMID: 28026041 Free PMC article. Review.
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy.
Finkel RS, Mercuri E, Darras BT, Connolly AM, Kuntz NL, Kirschner J, Chiriboga CA, Saito K, Servais L, Tizzano E, Topaloglu H, Tulinius M, Montes J, Glanzman AM, Bishop K, Zhong ZJ, Gheuens S, Bennett CF, Schneider E, Farwell W, De Vivo DC; ENDEAR Study Group. Finkel RS, et al. N Engl J Med. 2017 Nov 2;377(18):1723-1732. doi: 10.1056/NEJMoa1702752. N Engl J Med. 2017. PMID: 29091570 Free article. Clinical Trial.
New and developing therapies in spinal muscular atrophy.
Kariyawasam D, Carey KA, Jones KJ, Farrar MA. Kariyawasam D, et al. Among authors: farrar ma. Paediatr Respir Rev. 2018 Sep;28:3-10. doi: 10.1016/j.prrv.2018.03.003. Epub 2018 Apr 5. Paediatr Respir Rev. 2018. PMID: 29703692 Review.
Growth and nutrition in pediatric neuromuscular disorders.
Chou E, Lindeback R, D'Silva AM, Sampaio H, Neville K, Farrar MA. Chou E, et al. Among authors: farrar ma. Clin Nutr. 2021 Jun;40(6):4341-4348. doi: 10.1016/j.clnu.2021.01.013. Epub 2021 Jan 22. Clin Nutr. 2021. PMID: 33551221
224 results