Dual Supramolecular Nanoparticle Vectors Enable CRISPR/Cas9-Mediated Knockin of Retinoschisin 1 Gene-A Potential Nonviral Therapeutic Solution for X-Linked Juvenile Retinoschisis.
Chou SJ, Yang P, Ban Q, Yang YP, Wang ML, Chien CS, Chen SJ, Sun N, Zhu Y, Liu H, Hui W, Lin TC, Wang F, Zhang RY, Nguyen VQ, Liu W, Chen M, Jonas SJ, Weiss PS, Tseng HR, Chiou SH.
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Adv Sci (Weinh). 2020 Apr 16;7(10):1903432. doi: 10.1002/advs.201903432. eCollection 2020 May.
Adv Sci (Weinh). 2020.
PMID: 32440478
Free PMC article.