McCarty D - Search Results

1

Durability of transgene expression after rAAV gene therapy.

Muhuri M, Levy DI, Schulz M, McCarty D, Gao G. Muhuri M, et al. Among authors: mccarty d. Mol Ther. 2022 Apr 6;30(4):1364-1380. doi: 10.1016/j.ymthe.2022.03.004. Epub 2022 Mar 10. Mol Ther. 2022. PMID: 35283274 Free PMC article. Review.

2

Evaluating the state of the science for adeno-associated virus integration: An integrated perspective.

Sabatino DE, Bushman FD, Chandler RJ, Crystal RG, Davidson BL, Dolmetsch R, Eggan KC, Gao G, Gil-Farina I, Kay MA, McCarty DM, Montini E, Ndu A, Yuan J; American Society of Gene and Cell Therapy (ASGCT) Working Group on AAV Integration. Sabatino DE, et al. Among authors: mccarty dm. Mol Ther. 2022 Aug 3;30(8):2646-2663. doi: 10.1016/j.ymthe.2022.06.004. Epub 2022 Jun 10. Mol Ther. 2022. PMID: 35690906 Free PMC article. Review.

3

Significantly increased lifespan and improved behavioral performances by rAAV gene delivery in adult mucopolysaccharidosis IIIB mice.

Fu H, Kang L, Jennings JS, Moy SS, Perez A, Dirosario J, McCarty DM, Muenzer J. Fu H, et al. Among authors: mccarty dm. Gene Ther. 2007 Jul;14(14):1065-77. doi: 10.1038/sj.gt.3302961. Epub 2007 Apr 26. Gene Ther. 2007. PMID: 17460717

4

Correction of neurological disease of mucopolysaccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery.

Fu H, Dirosario J, Killedar S, Zaraspe K, McCarty DM. Fu H, et al. Mol Ther. 2011 Jun;19(6):1025-33. doi: 10.1038/mt.2011.34. Epub 2011 Mar 8. Mol Ther. 2011. PMID: 21386820 Free PMC article.

5

Patterns of scAAV vector insertion associated with oncogenic events in a mouse model for genotoxicity.

Rosas LE, Grieves JL, Zaraspe K, La Perle KM, Fu H, McCarty DM. Rosas LE, et al. Mol Ther. 2012 Nov;20(11):2098-110. doi: 10.1038/mt.2012.197. Epub 2012 Sep 18. Mol Ther. 2012. PMID: 22990674 Free PMC article.

6

Biodistribution and Tolerability of AAV-PHP.B-CBh-SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles.

Palazzi X, Pardo ID, Sirivelu MP, Newman L, Kumpf SW, Qian J, Franks T, Lopes S, Liu J, Monarski L, Casinghino S, Ritenour C, Ritenour H, Dubois C, Olson J, Graves J, Alexander KE, Coskran T, Lanz TA, Brady J, McCarty D, Suryanarayan S, Whiteley LO. Palazzi X, et al. Among authors: mccarty d. Hum Gene Ther. 2022 Feb;33(3-4):175-187. doi: 10.1089/hum.2021.116. Hum Gene Ther. 2022. PMID: 34931542 Free PMC article.

7

Self-complementary AAV vectors; advances and applications.

McCarty DM. McCarty DM. Mol Ther. 2008 Oct;16(10):1648-56. doi: 10.1038/mt.2008.171. Epub 2008 Aug 5. Mol Ther. 2008. PMID: 18682697 Free article. Review.

8

Broad functional correction of molecular impairments by systemic delivery of scAAVrh74-hSGSH gene delivery in MPS IIIA mice.

Duncan FJ, Naughton BJ, Zaraspe K, Murrey DA, Meadows AS, Clark KR, Newsom DE, White P, Fu H, McCarty DM. Duncan FJ, et al. Mol Ther. 2015 Apr;23(4):638-47. doi: 10.1038/mt.2015.9. Epub 2015 Jan 16. Mol Ther. 2015. PMID: 25592334 Free PMC article.

9

Self-complementary adeno-associated virus serotype 2 vector: global distribution and broad dispersion of AAV-mediated transgene expression in mouse brain.

Fu H, Muenzer J, Samulski RJ, Breese G, Sifford J, Zeng X, McCarty DM. Fu H, et al. Mol Ther. 2003 Dec;8(6):911-7. doi: 10.1016/j.ymthe.2003.08.021. Mol Ther. 2003. PMID: 14664793 Free article.

10

Restoration of central nervous system alpha-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-associated viral type 2 vector delivery.

Fu H, DiRosario J, Kang L, Muenzer J, McCarty DM. Fu H, et al. J Gene Med. 2010 Jul;12(7):624-33. doi: 10.1002/jgm.1480. J Gene Med. 2010. PMID: 20603889

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