Search Page
Save citations to file
Email citations
Send citations to clipboard
Add to Collections
Add to My Bibliography
Create a file for external citation management software
Your saved search
Your RSS Feed
Search Results
8 results
Filters applied: . Clear all
Results are displayed in a computed author sort order.
The Results By Year timeline is not available.
Page 1
Promoterless, Nuclease-Free Genome Editing Confers a Growth Advantage for Corrected Hepatocytes in Mice With Methylmalonic Acidemia.
Hepatology. 2021 Jun;73(6):2223-2237. doi: 10.1002/hep.31570. Epub 2021 May 21.
Hepatology. 2021.
PMID: 32976669
Free PMC article.
Genome editing for inborn errors of metabolism: advancing towards the clinic.
Schneller JL, Lee CM, Bao G, Venditti CP.
Schneller JL, et al.
BMC Med. 2017 Feb 27;15(1):43. doi: 10.1186/s12916-017-0798-4.
BMC Med. 2017.
PMID: 28238287
Free PMC article.
Review.
Item in Clipboard
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia.
An D, Schneller JL, Frassetto A, Liang S, Zhu X, Park JS, Theisen M, Hong SJ, Zhou J, Rajendran R, Levy B, Howell R, Besin G, Presnyak V, Sabnis S, Murphy-Benenato KE, Kumarasinghe ES, Salerno T, Mihai C, Lukacs CM, Chandler RJ, Guey LT, Venditti CP, Martini PGV.
An D, et al. Among authors: schneller jl.
Cell Rep. 2017 Dec 19;21(12):3548-3558. doi: 10.1016/j.celrep.2017.11.081.
Cell Rep. 2017.
PMID: 29262333
Free PMC article.
Item in Clipboard
In vivo genome editing at the albumin locus to treat methylmalonic acidemia.
Schneller JL, Lee CM, Venturoni LE, Chandler RJ, Li A, Myung S, Cradick TJ, Hurley AE, Lagor WR, Bao G, Venditti CP.
Schneller JL, et al.
Mol Ther Methods Clin Dev. 2021 Nov 11;23:619-632. doi: 10.1016/j.omtm.2021.11.004. eCollection 2021 Dec 10.
Mol Ther Methods Clin Dev. 2021.
PMID: 34901307
Free PMC article.
Item in Clipboard
Aberrant methylmalonylation underlies methylmalonic acidemia and is attenuated by an engineered sirtuin.
Head PE, Myung S, Chen Y, Schneller JL, Wang C, Duncan N, Hoffman P, Chang D, Gebremariam A, Gucek M, Manoli I, Venditti CP.
Head PE, et al. Among authors: schneller jl.
Sci Transl Med. 2022 May 25;14(646):eabn4772. doi: 10.1126/scitranslmed.abn4772. Epub 2022 May 25.
Sci Transl Med. 2022.
PMID: 35613279
Free PMC article.
Item in Clipboard
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia.
An D, Schneller JL, Frassetto A, Liang S, Zhu X, Park JS, Theisen M, Hong SJ, Zhou J, Rajendran R, Levy B, Howell R, Besin G, Presnyak V, Sabnis S, Murphy-Benenato KE, Kumarasinghe ES, Salerno T, Mihai C, Lukacs CM, Chandler RJ, Guey LT, Venditti CP, Martini PGV.
An D, et al. Among authors: schneller jl.
Cell Rep. 2018 Aug 28;24(9):2520. doi: 10.1016/j.celrep.2018.08.049.
Cell Rep. 2018.
PMID: 30157442
Free article.
No abstract available.
Item in Clipboard
Three-dimensional macroporous graphene scaffolds for tissue engineering.
Lalwani G, D'agati M, Gopalan A, Rao M, Schneller J, Sitharaman B.
Lalwani G, et al.
J Biomed Mater Res A. 2017 Jan;105(1):73-83. doi: 10.1002/jbm.a.35867. Epub 2016 Aug 27.
J Biomed Mater Res A. 2017.
PMID: 27529473
Item in Clipboard
Enrichment of transgene integrations by transient CRISPR activation of a silent reporter gene.
Mikkelsen NS, Hernandez SS, Jensen TI, Schneller JL, Bak RO.
Mikkelsen NS, et al. Among authors: schneller jl.
Mol Ther Methods Clin Dev. 2023 Feb 16;29:1-16. doi: 10.1016/j.omtm.2023.02.010. eCollection 2023 Jun 8.
Mol Ther Methods Clin Dev. 2023.
PMID: 36922985
Free PMC article.
Item in Clipboard
Cite
Cite