The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease.
Monaco A, Maffia V, Sorrentino NC, Sambri I, Ezhova Y, Giuliano T, Cacace V, Nusco E, De Risi M, De Leonibus E, Schrader T, Klärner FG, Bitan G, Fraldi A.
Monaco A, et al. Among authors: de risi m.
Mol Ther. 2022 Nov 2;30(11):3499. doi: 10.1016/j.ymthe.2022.10.001. Epub 2022 Oct 18.
Mol Ther. 2022.
PMID: 36261045
Free PMC article.
No abstract available.