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A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy.
Al-Zaidy SA, Lloyd-Puryear M, Kennedy A, Lopez V, Mendell JR. Al-Zaidy SA, et al. Among authors: mendell jr. Int J Neonatal Screen. 2017 Jun;3(2):8. doi: 10.3390/ijns3020008. Epub 2017 Apr 7. Int J Neonatal Screen. 2017. PMID: 31588416 Free PMC article.
Clinical Follow-Up for Duchenne Muscular Dystrophy Newborn Screening: A Proposal.
Kwon JM, Abdel-Hamid HZ, Al-Zaidy SA, Mendell JR, Kennedy A, Kinnett K, Cwik VA, Street N, Bolen J, Day JW, Connolly AM. Kwon JM, et al. Among authors: mendell jr. Muscle Nerve. 2016 Aug;54(2):186-91. doi: 10.1002/mus.25185. Epub 2016 Jun 13. Muscle Nerve. 2016. PMID: 27170260 Free PMC article.
Gene therapy for muscular dystrophy: moving the field forward.
Al-Zaidy S, Rodino-Klapac L, Mendell JR. Al-Zaidy S, et al. Among authors: mendell jr. Pediatr Neurol. 2014 Nov;51(5):607-18. doi: 10.1016/j.pediatrneurol.2014.08.002. Epub 2014 Aug 7. Pediatr Neurol. 2014. PMID: 25439576 Free PMC article. Review.
A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.
Mendell JR, Sahenk Z, Malik V, Gomez AM, Flanigan KM, Lowes LP, Alfano LN, Berry K, Meadows E, Lewis S, Braun L, Shontz K, Rouhana M, Clark KR, Rosales XQ, Al-Zaidy S, Govoni A, Rodino-Klapac LR, Hogan MJ, Kaspar BK. Mendell JR, et al. Mol Ther. 2015 Jan;23(1):192-201. doi: 10.1038/mt.2014.200. Epub 2014 Oct 17. Mol Ther. 2015. PMID: 25322757 Free PMC article. Clinical Trial.
A slowly progressive form of limb-girdle muscular dystrophy type 2C associated with founder mutation in the SGCG gene in Puerto Rican Hispanics.
Al-Zaidy SA, Malik V, Kneile K, Rosales XQ, Gomez AM, Lewis S, Hashimoto S, Gastier-Foster J, Kang P, Darras B, Kunkel L, Carlo J, Sahenk Z, Moore SA, Pyatt R, Mendell JR. Al-Zaidy SA, et al. Among authors: mendell jr. Mol Genet Genomic Med. 2015 Mar;3(2):92-8. doi: 10.1002/mgg3.125. Epub 2015 Jan 8. Mol Genet Genomic Med. 2015. PMID: 25802879 Free PMC article.
Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion.
Mendell JR, Chicoine LG, Al-Zaidy SA, Sahenk Z, Lehman K, Lowes L, Miller N, Alfano L, Galliers B, Lewis S, Murrey D, Peterson E, Griffin DA, Church K, Cheatham S, Cheatham J, Hogan MJ, Rodino-Klapac LR. Mendell JR, et al. Hum Gene Ther. 2019 Jul;30(7):794-801. doi: 10.1089/hum.2019.006. Epub 2019 Apr 19. Hum Gene Ther. 2019. PMID: 30838895 Free PMC article.
408 results