Large variation in effects during 10 years of enzyme therapy in adults with Pompe disease.
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Neurology. 2019 Nov 5;93(19):e1756-e1767. doi: 10.1212/WNL.0000000000008441. Epub 2019 Oct 16.
Neurology. 2019.
PMID: 31619483
Free PMC article.