Double-blind, randomized and controlled trial of EPI-743 in Friedreich's ataxia.
Zesiewicz T, Salemi JL, Perlman S, Sullivan KL, Shaw JD, Huang Y, Isaacs C, Gooch C, Lynch DR, Klein MB.
Zesiewicz T, et al.
Neurodegener Dis Manag. 2018 Aug;8(4):233-242. doi: 10.2217/nmt-2018-0013. Epub 2018 Jul 27.
Neurodegener Dis Manag. 2018.
PMID: 30051753
Clinical Trial.