Artificial miRNAs targeting CAG repeat expansion in ORFs cause rapid deadenylation and translation inhibition of mutant transcripts.
Ciesiolka A, Stroynowska-Czerwinska A, Joachimiak P, Ciolak A, Kozlowska E, Michalak M, Dabrowska M, Olejniczak M, Raczynska KD, Zielinska D, Wozna-Wysocka M, Krzyzosiak WJ, Fiszer A.
Ciesiolka A, et al. Among authors: krzyzosiak wj.
Cell Mol Life Sci. 2021 Feb;78(4):1577-1596. doi: 10.1007/s00018-020-03596-7. Epub 2020 Jul 21.
Cell Mol Life Sci. 2021.
PMID: 32696070
Free PMC article.