Sands MS - Search Results

1

Combination therapies for lysosomal storage disease: is the whole greater than the sum of its parts?

Hawkins-Salsbury JA, Reddy AS, Sands MS. Hawkins-Salsbury JA, et al. Among authors: sands ms. Hum Mol Genet. 2011 Apr 15;20(R1):R54-60. doi: 10.1093/hmg/ddr112. Epub 2011 Mar 19. Hum Mol Genet. 2011. PMID: 21421999 Free PMC article. Review.

2

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

Daly TM, Vogler C, Levy B, Haskins ME, Sands MS. Daly TM, et al. Among authors: sands ms. Proc Natl Acad Sci U S A. 1999 Mar 2;96(5):2296-300. doi: 10.1073/pnas.96.5.2296. Proc Natl Acad Sci U S A. 1999. PMID: 10051635 Free PMC article.

3

Murine mucopolysaccharidosis VIL: impact of therapies on the phenotype, clinical course, and pathology in a model of a lysosomal storage disease.

Vogler C, Barker J, Sands MS, Levy B, Galvin N, Sly WS. Vogler C, et al. Among authors: sands ms. Pediatr Dev Pathol. 2001 Sep-Oct;4(5):421-33. doi: 10.1007/s10024001-0079-1. Pediatr Dev Pathol. 2001. PMID: 11779044 Review.

4

Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs.

Mango RL, Xu L, Sands MS, Vogler C, Seiler G, Schwarz T, Haskins ME, Ponder KP. Mango RL, et al. Among authors: sands ms. Mol Genet Metab. 2004 May;82(1):4-19. doi: 10.1016/j.ymgme.2004.01.015. Mol Genet Metab. 2004. PMID: 15110316

5

Human CD34+ hematopoietic progenitor cell-directed lentiviral-mediated gene therapy in a xenotransplantation model of lysosomal storage disease.

Hofling AA, Devine S, Vogler C, Sands MS. Hofling AA, et al. Among authors: sands ms. Mol Ther. 2004 Jun;9(6):856-65. doi: 10.1016/j.ymthe.2004.03.013. Mol Ther. 2004. PMID: 15194052 Free article.

6

AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.

Hennig AK, Ogilvie JM, Ohlemiller KK, Timmers AM, Hauswirth WW, Sands MS. Hennig AK, et al. Among authors: sands ms. Mol Ther. 2004 Jul;10(1):106-16. doi: 10.1016/j.ymthe.2004.03.018. Mol Ther. 2004. PMID: 15233947 Free article.

7

Gene therapy for lysosomal storage diseases.

Daly TM, Sands MS. Daly TM, et al. Among authors: sands ms. Expert Opin Investig Drugs. 1998 Oct;7(10):1673-82. doi: 10.1517/13543784.7.10.1673. Expert Opin Investig Drugs. 1998. PMID: 15991909

8

Gene therapy for lysosomal storage diseases.

Sands MS, Davidson BL. Sands MS, et al. Mol Ther. 2006 May;13(5):839-49. doi: 10.1016/j.ymthe.2006.01.006. Epub 2006 Mar 20. Mol Ther. 2006. PMID: 16545619 Free article. Review.

9

Lysosomal dysfunction results in altered energy balance.

Woloszynek JC, Coleman T, Semenkovich CF, Sands MS. Woloszynek JC, et al. Among authors: sands ms. J Biol Chem. 2007 Dec 7;282(49):35765-71. doi: 10.1074/jbc.M705124200. Epub 2007 Oct 2. J Biol Chem. 2007. PMID: 17911106 Free article.

10

CNS-directed gene therapy for lysosomal storage diseases.

Sands MS, Haskins ME. Sands MS, et al. Acta Paediatr. 2008 Apr;97(457):22-7. doi: 10.1111/j.1651-2227.2008.00660.x. Acta Paediatr. 2008. PMID: 18339183 Free PMC article. Review.

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