The site-specific correction of genetic defects

Nat Med. 1998 Mar;4(3):274-5. doi: 10.1038/nm0398-274.
No abstract available

Publication types

  • Comment
  • News

MeSH terms

  • Animals
  • Asialoglycoprotein Receptor
  • Blood Coagulation / genetics
  • Drug Compounding
  • Factor IX / genetics*
  • Gene Targeting / methods*
  • Liver / drug effects*
  • Mutagenesis, Site-Directed*
  • Oligodeoxyribonucleotides
  • Oligonucleotides / pharmacology*
  • Oligoribonucleotides
  • Rats
  • Receptors, Cell Surface / metabolism

Substances

  • Asialoglycoprotein Receptor
  • Oligodeoxyribonucleotides
  • Oligonucleotides
  • Oligoribonucleotides
  • Receptors, Cell Surface
  • Factor IX