Monitoring gene therapy with cytosine deaminase: in vitro studies using tritiated-5-fluorocytosine

J Nucl Med. 1996 Jan;37(1):87-94.

Abstract

Genetically modified mammalian cells that express the cytosine deaminase (CD) gene are able to convert the nontoxic prodrug 5-fluorocytosine (5-FC) to the toxic metabolite 5-fluorouracil (5-FU). PET with 18F-5-FC may be used for in vivo measurement of CD activity in genetically modified tumors.

Methods: A human glioblastoma cell line was stably transfected with the Escherichia coli CD gene. After incubation of lysates of CD-expressing cells and control cells with 3H-5-FC high-performance liquid chromatography (HPLC) was performed. The uptake of 5-FC was measured after various incubation times using therapeutic amounts of 5-FC. In addition, saturation and competition experiments with 5-FC and 5-FU were performed. Finally, the efflux was measured.

Results: We found that 3H-5-FU was produced in CD-expressing cells, whereas in the control cells only 3H-5-FC was detected. Moreover, significant amounts of 5-FU were found in the medium of cultured cells, which may account for the bystander effect observed in previous experiments. However, uptake studies revealed a moderate and nonsaturable accumulation of radioactivity in the tumor cells, suggesting that 5-FC enters the cells only through diffusion. Although a significant difference in 5-FC uptake was seen between CD-positive and control cells after 48 hr of incubation, no difference was observed after 2 hr of incubation. Furthermore, a rapid efflux could be demonstrated.

Conclusion: 5-Fluorocytosine transport may be a limiting factor for this therapeutic procedure. Quantitation with PET has to rely more on dynamic studies and modeling, including HPLC analysis of the plasma, than on nonmodeling approaches.

MeSH terms

  • Chromatography, High Pressure Liquid
  • Cytosine Deaminase
  • Flucytosine / pharmacokinetics
  • Flucytosine / therapeutic use*
  • Fluorouracil / metabolism
  • Fluorouracil / therapeutic use*
  • Genetic Therapy / methods*
  • Glioblastoma / metabolism
  • Glioblastoma / therapy*
  • Humans
  • In Vitro Techniques
  • Nucleoside Deaminases / genetics
  • Nucleoside Deaminases / metabolism*
  • Prodrugs / pharmacokinetics
  • Prodrugs / therapeutic use*
  • Tomography, Emission-Computed
  • Transfection
  • Tritium
  • Tumor Cells, Cultured

Substances

  • Prodrugs
  • Tritium
  • Flucytosine
  • Nucleoside Deaminases
  • Cytosine Deaminase
  • Fluorouracil