Innovative methodologies for rare diseases clinical trials

Orphanet J Rare Dis. 2024 May 7;19(1):190. doi: 10.1186/s13023-024-03189-8.

Authors

Rima Nabbout^{1

2

3}, Ralf-Dieter Hilgers⁴

Affiliations

¹ Reference centre for rare epilepsies Université Paris cité, Paris, France. rima.nabbout@aphp.fr.
² Assistance Publique-Hôpitaux de Paris, Hôpital Necker-Enfants Malades, Paris, France. rima.nabbout@aphp.fr.
³ Institut Imagine, INSERM U1163, Paris, France. rima.nabbout@aphp.fr.
⁴ RWTH Aachen University, Institute of Medical Statistics, 52074, Aachen, Germany. rhilgers@ukaachen.de.

No abstract available

Publication types

Editorial

MeSH terms

Clinical Trials as Topic*
Humans
Rare Diseases*