AAV gene therapy to treat Friedreich's ataxia cardiomyopathy

Lab Anim (NY). 2024 Apr;53(4):86. doi: 10.1038/s41684-024-01351-0.
No abstract available

MeSH terms

  • Cardiomyopathies* / genetics
  • Cardiomyopathies* / therapy
  • Frataxin
  • Friedreich Ataxia* / genetics
  • Friedreich Ataxia* / therapy
  • Humans

Substances

  • Frataxin