Base editing effectively prevents early-onset severe cardiomyopathy in Mybpc3 mutant mice

Cell Res. 2024 Apr;34(4):327-330. doi: 10.1038/s41422-024-00930-7. Epub 2024 Feb 9.
No abstract available

Publication types

  • Letter

MeSH terms

  • Animals
  • Cardiomyopathies* / genetics
  • Cardiomyopathies* / prevention & control
  • Gene Editing*
  • Genotype
  • Mice
  • Mutation / genetics
  • Phenotype