KIT-mutated pediatric core-binding factor systemic mastocytosis-acute myeloid leukemia treated with avapritinib and decitabine

Pediatr Blood Cancer. 2024 Apr;71(4):e30898. doi: 10.1002/pbc.30898. Epub 2024 Jan 30.
No abstract available

Publication types

  • Letter

MeSH terms

  • Child
  • Core Binding Factors
  • Decitabine
  • Humans
  • Leukemia, Myeloid, Acute* / drug therapy
  • Leukemia, Myeloid, Acute* / genetics
  • Mastocytosis, Systemic*
  • Mutation
  • Proto-Oncogene Proteins c-kit / genetics
  • Pyrazoles*
  • Pyrroles*
  • Triazines*

Substances

  • avapritinib
  • Decitabine
  • Core Binding Factors
  • Proto-Oncogene Proteins c-kit
  • Pyrazoles
  • Pyrroles
  • Triazines