First in vivo base-editing trial shows promise

Mol Ther. 2024 Jan 3;32(1):1-2. doi: 10.1016/j.ymthe.2023.12.001. Epub 2023 Dec 16.

Author

Renzhi Han¹

Affiliation

¹ Department of Pediatrics, Herman B. Wells Center for Pediatric Research, Indiana University School of Medicine, 980 W Walnut St Joseph E. Walther Hall (R3) C118, Indianapolis, IN 46202, USA. Electronic address: rh11@iu.edu.

PMID: 38104562
PMCID: PMC10787164 (available on 2025-01-03)
DOI: 10.1016/j.ymthe.2023.12.001

No abstract available

Publication types

Editorial

MeSH terms

CRISPR-Cas Systems*
Gene Editing*

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