Crossing the gates of Babylon: Brain-penetrating enzyme replacement for lysosomal disorders
Mol Ther Methods Clin Dev
.
2023 Aug 10:30:315-316.
doi: 10.1016/j.omtm.2023.07.008.
eCollection 2023 Sep 14.
Author
Guilherme Baldo
1
2
Affiliations
1
Departamento de Fisiologia, Universidade Federal do Rio Grande do Sul, Porto Alegre, Rio Grande do Sul 90035-903, Brazil.
2
Casa dos Raros, R. São Manoel, 730 Santa Cecília, Porto Alegre, RS 90610-261, Brazil.
PMID:
37637386
PMCID:
PMC10447917
DOI:
10.1016/j.omtm.2023.07.008
No abstract available
Publication types
News