1 Center for Gene Therapy, Abigail Wexner Research Institute Nationwide Children's Hospital and Department of Pediatrics, The Ohio State University, Columbus, OH, United States.
2 Department of Pediatrics, Indiana University, Indianapolis, IN, United States.
3 Horae Gene Therapy Center, Department of Microbiology and Physiological Systems, University of Massachusetts Chan Medical School, Worcester, MA, United States.
4 Department of Research & Discovery, Genemagic Biosciences, Philadelphia, PA, United States.
5 Department of Pediatrics, University of Minnesota, Minneapolis, MN, United States.