CRISPR-Cas9 in hiPSCs: A new era in personalized treatment for Stargardt disease

Mol Ther Nucleic Acids. 2023 May 27:32:896-897. doi: 10.1016/j.omtn.2023.05.008. eCollection 2023 Jun 13.

Authors

Soujanya Kuntam¹, Pradeep Reddy Cingaram²

Affiliations

¹ Institute of Plant Biology, Biological Research Centre, Szeged, Temesvári krt. 62, 6726 Szeged, Hungary.
² Department of Human Genetics, Sylvester Comprehensive Cancer Center, University of Miami Miller School of Medicine, Miami, FL 33136, USA.

No abstract available

Keywords: ABCA4 gene; CRISPR-Cas9; IRD; STGD1; Stargardt disease; gene editing; hiPSC; inherited retinal dystrophies.

Publication types

News