Retrospective Real-Life Data, Efficacy and Safety of Vismodegib Treatment in Patients with Advanced and Multiple Basal Cell Carcinoma: 3-Year Experience from a Spanish Center

Int J Environ Res Public Health. 2023 May 15;20(10):5824. doi: 10.3390/ijerph20105824.

Abstract

Background: Basal cell carcinoma (BCC) is the most common type of skin cancer and can represent a therapeutic challenge in patients with locally advanced disease. Vismodegib is a hedgehog pathway inhibitor approved by the FDA for use in this type of tumor. We present a case series to describe our experience with the use of vismodegib.

Methods: A retrospective study that included patients treated with vismodegib at our dermatology unit was conducted. Monthly follow-up was performed, and we registered the clinical evolution and adverse reactions.

Results: A total of six patients with locally advanced BCCs were included (50% males and 50% females), with a mean age of 78.5 years old. The treatment was administered over a mean of 5 months. A complete response was observed in four cases and partial response in two cases. No recurrence was detected, with a median follow-up duration after discontinuation of 18 months. Most patients (83%) had at least one adverse event, and two needed dose adjustment temporarily or permanently to continue. The main adverse effect was muscle spasms (66.7%). The main limitation of our study was the small sample, which was not representative of the general population.

Conclusions: Vismodegib is a safe and effective treatment for locally advanced BCC, and its role in unresectable BCC seems to be an important option in these challenging cases.

Keywords: hedgehog inhibitor; locally advanced basal cell carcinoma; nonmelanoma skin cancer; vismodegib.

Publication types

  • Case Reports

MeSH terms

  • Aged
  • Antineoplastic Agents* / adverse effects
  • Carcinoma, Basal Cell* / drug therapy
  • Female
  • Hedgehog Proteins
  • Humans
  • Male
  • Retrospective Studies
  • Skin Neoplasms* / chemically induced
  • Skin Neoplasms* / drug therapy

Substances

  • HhAntag691
  • Hedgehog Proteins
  • Antineoplastic Agents

Supplementary concepts

  • Basal cell carcinoma, multiple

Grants and funding

This research received no external funding.