Mitapivat for treatment of pyruvate kinase deficiency

Lancet Haematol. 2022 Oct;9(10):e708-e709. doi: 10.1016/S2352-3026(22)00249-6. Epub 2022 Aug 18.
No abstract available

Publication types

  • Comment

MeSH terms

  • Anemia, Hemolytic, Congenital Nonspherocytic* / drug therapy
  • Erythrocytes
  • Humans
  • Piperazines
  • Pyruvate Kinase / deficiency
  • Pyruvate Metabolism, Inborn Errors* / drug therapy
  • Quinolines

Substances

  • Piperazines
  • Quinolines
  • mitapivat
  • Pyruvate Kinase

Supplementary concepts

  • Pyruvate Kinase Deficiency of Red Cells