Editorial: Lessons Learned from Translational Research in Neuromuscular Diseases: Impact on Study Design, Outcome Measures and Managing Expectation

Anna G Mayhew; Leslie Nelson; Michela Guglieri; Tracey Willis

doi:10.3389/fgene.2022.840074

Editorial: Lessons Learned from Translational Research in Neuromuscular Diseases: Impact on Study Design, Outcome Measures and Managing Expectation

Front Genet. 2022 Jul 4:13:840074. doi: 10.3389/fgene.2022.840074. eCollection 2022.

Authors

Anna G Mayhew¹, Leslie Nelson², Michela Guglieri¹, Tracey Willis³

Affiliations

¹ The John Walton Muscular Dystrophy Research Centre, Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom.
² Department of Physical Therapy, University of Texas Southwestern Medical Center, Dallas, TX, United States.
³ Robert Jones and Agnes Hunt Orthopaedic Hospital, NHS Foundation Trust, Oswestry, England.

No abstract available

Keywords: clinical outcome assessments; clinical trial; duchenne muscular dystrophy (DMD); neuromuscular disorders (NMD); remote assessment; spinal muscular atrophy (SMA).

Publication types

Editorial