Genetic validation of Aspergillus fumigatus phosphoglucomutase as a viable therapeutic target in invasive aspergillosis

J Biol Chem. 2022 Jun;298(6):102003. doi: 10.1016/j.jbc.2022.102003. Epub 2022 Apr 30.

Abstract

Aspergillus fumigatus is the causative agent of invasive aspergillosis, an infection with mortality rates of up to 50%. The glucan-rich cell wall of A. fumigatus is a protective structure that is absent from human cells and is a potential target for antifungal treatments. Glucan is synthesized from the donor uridine diphosphate glucose, with the conversion of glucose-6-phosphate to glucose-1-phosphate by the enzyme phosphoglucomutase (PGM) representing a key step in its biosynthesis. Here, we explore the possibility of selectively targeting A. fumigatus PGM (AfPGM) as an antifungal treatment strategy. Using a promoter replacement strategy, we constructed a conditional pgm mutant and revealed that pgm is required for A. fumigatus growth and cell wall integrity. In addition, using a fragment screen, we identified the thiol-reactive compound isothiazolone fragment of PGM as targeting a cysteine residue not conserved in the human ortholog. Furthermore, through scaffold exploration, we synthesized a para-aryl derivative (ISFP10) and demonstrated that it inhibits AfPGM with an IC50 of 2 μM and exhibits 50-fold selectivity over the human enzyme. Taken together, our data provide genetic validation of PGM as a therapeutic target and suggest new avenues for inhibiting AfPGM using covalent inhibitors that could serve as tools for chemical validation.

Keywords: Aspergillus fumigatus; FBDD; antifungal; covalent inhibitor; fragment; isothiazolone; phosphoglucomutase.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antifungal Agents / pharmacology
  • Aspergillosis* / drug therapy
  • Aspergillosis* / microbiology
  • Aspergillus fumigatus* / enzymology
  • Aspergillus fumigatus* / genetics
  • Glucans / metabolism
  • Humans
  • Phosphoglucomutase / genetics
  • Phosphoglucomutase / metabolism

Substances

  • Antifungal Agents
  • Glucans
  • Phosphoglucomutase